Gema
Rebolleda Fernández
Profesor/a Titular Universidad
German Center for Neurodegenerative Diseases
Bonn, AlemaniaPublications en collaboration avec des chercheurs de German Center for Neurodegenerative Diseases (2)
2023
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Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G>A MT-ND4 Mutation
Ophthalmology and Therapy, Vol. 12, Núm. 1, pp. 401-429
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Safety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy
American Journal of Ophthalmology, Vol. 249, pp. 108-125