Comprehensive long-term efficacy and safety of recombinant human alpha-mannosidase (velmanase alfa) treatment in patients with alpha-mannosidosis

  1. Lund, A.M.
  2. Borgwardt, L.
  3. Cattaneo, F.
  4. Ardigò, D.
  5. Geraci, S.
  6. Gil-Campos, M.
  7. De Meirleir, L.
  8. Laroche, C.
  9. Dolhem, P.
  10. Cole, D.
  11. Tylki-Szymanska, A.
  12. Lopez-Rodriguez, M.
  13. Guillén-Navarro, E.
  14. Dali, C.I.
  15. Héron, B.
  16. Fogh, J.
  17. Muschol, N.
  18. Phillips, D.
  19. Van den Hout, J.M.H.
  20. Jones, S.A.
  21. Amraoui, Y.
  22. Harmatz, P.
  23. Guffon, N.
Journal:
Journal of Inherited Metabolic Disease

ISSN: 1573-2665 0141-8955

Year of publication: 2018

Volume: 41

Issue: 6

Pages: 1225-1233

Type: Article

DOI: 10.1007/S10545-018-0175-2 GOOGLE SCHOLAR lock_openOpen access editor

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