Publications en collaboration avec des chercheurs de Icahn School of Medicine at Mount Sinai (4)

2023

  1. Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G>A MT-ND4 Mutation

    Ophthalmology and Therapy, Vol. 12, Núm. 1, pp. 401-429

  2. Randomized trial of bilateral gene therapy injection for m.11778G>A MT-ND4 Leber optic neuropathy

    Brain : a journal of neurology, Vol. 146, Núm. 4, pp. 1328-1341

  3. Safety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy

    American Journal of Ophthalmology, Vol. 249, pp. 108-125

2022

  1. Study design and baseline characteristics for the reflect gene therapy trial ofm.11778g>A/ ND4-LHON

    BMJ Open Ophthalmology, Vol. 7, Núm. 1