Gema
Rebolleda Fernández
Profesor/a Titular Universidad
Ghent University
Gante, BélgicaGhent University-ko ikertzaileekin lankidetzan egindako argitalpenak (2)
2023
-
Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G>A MT-ND4 Mutation
Ophthalmology and Therapy, Vol. 12, Núm. 1, pp. 401-429
2022
-
Study design and baseline characteristics for the reflect gene therapy trial ofm.11778g>A/ ND4-LHON
BMJ Open Ophthalmology, Vol. 7, Núm. 1