Publicaciones en colaboración con investigadores/as de Great Ormond Street Hospital (1)

2024

  1. Effects of oral sepiapterin on blood Phe concentration in a broad range of patients with phenylketonuria (APHENITY): results of an international, phase 3, randomised, double-blind, placebo-controlled trial

    The Lancet, Vol. 404, Núm. 10460, pp. 1333-1345