Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G>A MT-ND4 Mutation

  1. Carelli, V.
  2. Newman, N.J.
  3. Yu-Wai-Man, P.
  4. Biousse, V.
  5. Moster, M.L.
  6. Subramanian, P.S.
  7. Vignal-Clermont, C.
  8. Wang, A.-G.
  9. Donahue, S.P.
  10. Leroy, B.P.
  11. Sergott, R.C.
  12. Klopstock, T.
  13. Sadun, A.A.
  14. Rebolleda Fernández, G.
  15. Chwalisz, B.K.
  16. Banik, R.
  17. Girmens, J.F.
  18. La Morgia, C.
  19. DeBusk, A.A.
  20. Jurkute, N.
  21. Priglinger, C.
  22. Karanjia, R.
  23. Josse, C.
  24. Salzmann, J.
  25. Montestruc, F.
  26. Roux, M.
  27. Taiel, M.
  28. Sahel, J.-A.
  29. Carelli, V.
  30. Barboni, P.
  31. Carbonelli, M.
  32. Di Vito, L.
  33. Amore, G.
  34. Contin, M.
  35. Mohamed, S.
  36. Silvestri, S.
  37. D’Agati, P.
  38. Newman, N.J.
  39. Biousse, V.
  40. Hubbard, G.B.
  41. O’Keefe, G.
  42. Hendrick, A.M.
  43. Dattilo, M.
  44. Peragallo, J.H.
  45. Hawy, E.
  46. DuBois, L.
  47. Gibbs, D.
  48. Filho, A.F.
  49. Dobbs, J.
  50. Acheson, J.
  51. Boston, H.
  52. Eleftheriadou, M.
  53. Esposti, S.
  54. Gemenetzi, M.
  55. Leitch-Devlin, L.
  56. Tucker, W.R.
  57. Burale, A.
  58. Anand, S.
  59. Memon, M.A.
  60. Hussain, R.
  61. Jorany, R.
  62. Sheel, P.
  63. SantaMaria, M.
  64. Tollis, H.
  65. Haller, J.A.
  66. Massini, M.
  67. Pecen, P.
  68. Mathias, M.
  69. Preston, M.
  70. Cho, S.
  71. Sahel, J.A.
  72. Hage, R.
  73. Plaine, L.
  74. Khemliche, W.
  75. Cheng, H.-C.
  76. Chen, C.
  77. Hwang, J.-M.
  78. Sun, C.
  79. Donahue, S.
  80. Patel, S.
  81. Gangaputra, S.
  82. Barrett, M.
  83. Ruark, S.
  84. Wilkins, S.
  85. De Zaeytijd, J.
  86. Van Cauwenbergh, C.
  87. Verhauwen, H.
  88. Catarino, C.B.
  89. Priglinger, S.
  90. Rudolph, G.
  91. von Livonius Bettina, S.T.
  92. Muth, D.
  93. Wolf, A.
  94. Al-Tamami, J.
  95. Pressler, A.
  96. Schertler, C.
  97. Hildebrandt, M.
  98. Neuenhahn, M.
  99. Heilweil, G.
  100. Tsui, I.
  101. Urquijo, L.J.
  102. Negrete Muñoz, F.J.
  103. Fortin, E.
  104. Cestari, D.
  105. Tai, K.
  106. Castillo, L.
  107. Garcia, V.
  108. Bandello, A.M.F.
  109. Barboni, P.
  110. Cascavilla, M.L.
  111. Battista, M.
  112. Calcagno, F.
  113. Pina, A.
  114. Leruez, S.
  115. Forooza, R.
  116. Montrer des auteurs +
Revue:
Ophthalmology and Therapy

ISSN: 2193-6528 2193-8245

Année de publication: 2023

Volumen: 12

Número: 1

Pages: 401-429

Type: Article

DOI: 10.1007/S40123-022-00611-X GOOGLE SCHOLAR lock_openAccès ouvert editor